Rocket Pharmaceuticals is a biotechnology company focused on seeking cures through molecular and gene therapy. It develops treatments for patients with rare and often devastating orphan diseases using a lentiviral-based gene therapy approach. The Company works in partnerships with a number of international research institutions as well as with centers of manufacturing and cell processing expertise, and leads research, development, clinical and regulatory programs. It aims to launch and globally commercialize innovative gene therapies in disease areas with high unmet need.